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dc.contributor.authorAnderson, L Jen
dc.contributor.authorHenley, Wen
dc.contributor.authorWyatt, K Men
dc.contributor.authorNikolaou, Ven
dc.contributor.authorWaldek, Sen
dc.contributor.authorHughes, D Aen
dc.contributor.authorLachmann, R Hen
dc.contributor.authorLogan, Stuarten
dc.date.accessioned2016-08-05T13:15:11Z
dc.date.available2016-08-05T13:15:11Z
dc.date.issued2014-11
dc.identifier.citationEffectiveness of enzyme replacement therapy in adults with late-onset Pompe disease: results from the NCS-LSD cohort study. 2014, 37 (6):945-52 J. Inherit. Metab. Dis.en
dc.identifier.issn1573-2665
dc.identifier.pmid24906254
dc.identifier.doi10.1007/s10545-014-9728-1
dc.identifier.urihttp://hdl.handle.net/11287/617981
dc.description.abstractTo determine the effectiveness of enzyme replacement therapy (ERT) for adults with late-onset Pompe disease.en
dc.language.isoenen
dc.publisherSpringeren
dc.relation.urlhttp://dx.doi.org/10.1007/s10545-014-9728-1en
dc.rightsArchived with thanks to Journal of inherited metabolic diseaseen
dc.subjectWessex Classification Subject Headings::Paediatricsen
dc.titleEffectiveness of enzyme replacement therapy in adults with late-onset Pompe disease: results from the NCS-LSD cohort study.en
dc.typeJournal Articleen
dc.typeMulticenter Studyen
dc.typeObservational Studyen
dc.typeResearch Support, Non-U.S. Gov'ten
dc.identifier.journalJournal of inherited metabolic diseaseen
dc.type.versionPublisheden


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